Novel Biomanufacturing of AAV Platform

Overview

Adeno-associated virus (AAV) is an unenveloped virus classified in the Parvoviridae family, known for its ability to effectively and securely transport genetic material into cells, making it valuable for gene therapy. Although industrial manufacturing methods for AAV vector production have advanced, challenges remain in terms of quality and production costs, hindering wider development. The limited scalability of current methods has resulted in prohibitively high costs for many patients seeking AAV gene therapy. We aim to develop a highly cost effective solution to produce the world’s most important gene therapy vector.